Current treatment options |
Geen geneesmiddel voor DMD, huidige behandeling: "best supportive care (BSC)". |
Therapeutic value |
No judgement yet |
Substantiation |
Informatie door de fabrikant aangeleverd op basis van: EMA guidance 2015; Birnkrant, et al. Lancet Neurol 2018;17:251-267; Birnkrant, et al. Lancet Neurol 2018;17:347-361; Birnkrant, et al. Lancet Neurol 2018;17:445-455. |
Duration of treatment |
continuous |
Frequency of administration |
1 times a week |
Dosage per administration |
30 mg/kg |
References |
NCT02420379, Mendell, et al. Ann Neurol 2013;74:637–647;
Mendell, et al. Ann Neurol 2016;79:257-71. |