Extended indication Essential thrombocythaemia and myelofibrosis.
Therapeutic value No estimate possible yet
Registration phase Clinical trials

Product

Active substance Bomedemstat
Domain Hematology
Reason of inclusion New medicine (specialité)
Main indication Myeloproliferative disorders
Extended indication Essential thrombocythaemia and myelofibrosis.
Manufacturer Imago
Mechanism of action Unknown
Route of administration Oral
Therapeutical formulation Capsule
Budgetting framework Intermural (MSZ)
Additional remarks Lysine specific demethylase 1 inhibitor.

Registration

Registration route Centralised (EMA)
Type of trajectory Unknown
Particularity Unknown
ATMP No
Submission date 2024
Expected Registration 2025
Orphan drug Yes
Registration phase Clinical trials

Therapeutic value

Therapeutic value No estimate possible yet

This assessment does not indicate any potential inclusion in the package.

Frequency of administration 1 times a day
References NCT05223920

Expected patient volume per year

Patient volume < 166

Market share is generally not included unless otherwise stated.

References NKR 2018 (1);
Additional remarks In totaal waren er 166 diagnoses in 2018 (1).

Expected cost per patient per year

Potential total cost per year

Off label use

Off label use Unknown

Indication extension

Indication extensions Unknown

Other information