Extended indication Hyperphosphatemia
Therapeutic value No judgement
Total cost 39,045,600.00
Registration phase Clinical trials

Product

Active substance Tenapanor
Domain Metabolism and Endocrinology
Reason of inclusion Indication extension IND
Main indication Hormonal disorders
Extended indication Hyperphosphatemia
Manufacturer Ardelyx
Mechanism of action Unknown
Route of administration Oral
Therapeutical formulation Tablet
Budgetting framework Extramural (GVS)
Additional remarks Scrip pipeline watch 13 nov 2017: decreased potassium, well tolerated. "First-in-class inhibitor of gastrointestinal NHE3 sodium transporter reduces dietary sodium absorption".

Registration

Registration route Centralised (EMA)
Type of trajectory Unknown
Particularity Unknown
ATMP Unknown
Submission date 2019
Expected Registration 2020
Orphan drug No
Registration phase Clinical trials

Therapeutic value

Current treatment options Fosfaatbinders zoals sevelameer, ferrioxidesaccharaat, lanthaancarbonaat, calciumacetaat/​magnesiumcarbonaat
Therapeutic value No judgement

This assessment does not indicate any potential inclusion in the package.

References Farmacotherapeutisch kompas.

Expected patient volume per year

Patient volume < 11,832

Market share is generally not included unless otherwise stated.

References GIPdatabank
Additional remarks Aantal patiënten dat fosfaatbinders heeft gekregen in 2016 betreft 11.832.

Expected cost per patient per year

Cost 3,300.00

This amount gives an indication of the total cost. It is the result of the average expected patient volume times the average cost per patient. both per year.

References GIPdatabank
Additional remarks Vergoeding per gebruiker voor fosfaatbinders in 2016 betreft €3.292,39

Potential total cost per year

Total cost 39,045,600.00

Off label use

Off label use Unknown

Indication extension

Indication extensions Yes
Indication extensions Ook in PhIII voor de indicatie: "Constipation Predominant Irritable Bowel Syndrome".
References Scrip, clinicaltrials.gov.

Other information