Extended indication Ciclosporin in combination with standard therapy for the treatment of bronchiolitis obliterans syndrome in adults and the elderly after lung transplan
Therapeutic value No estimate possible yet
Registration phase No registration expected

Product

Active substance Ciclosporine
Domain Lung diseases
Reason of inclusion Indication extension IND
Main indication Lung diseases other
Extended indication Ciclosporin in combination with standard therapy for the treatment of bronchiolitis obliterans syndrome in adults and the elderly after lung transplantation.
Manufacturer Zambon
Route of administration Unknown
Therapeutical formulation Unknown
Budgetting framework Extramural (GVS)
Additional remarks Fabrikant: Zambon. Liposomale cyclosporine A voor inhalatie (L-CsA-i).

Registration

Registration route Centralised (EMA)
Type of trajectory Normal trajectory
ATMP No
Orphan drug Yes
Registration phase No registration expected
Additional remarks De fase 3-studie voor crinecerfont in het CAHtalyst Pediatric Study werd in 2023 afgerond. De combinatie van het middel en de indicatie werd in 2024 goedgekeurd door de FDA. In november 2025 was er nog geen aanvraag ingediend bij het EMA. Er wordt geen registratie verwacht.

Therapeutic value

Therapeutic value No estimate possible yet

This assessment does not indicate any potential inclusion in the package.

References NCT03657342 (BOSTON-1); NCT03656926 (BOSTON-2)

Expected patient volume per year

Patient volume

Market share is generally not included unless otherwise stated.

Expected cost per patient per year

Potential total cost per year

Off label use

Indication extension

Other information