Extended indication Treatment of monocarboxylate transporter 8 (MCT8) deficiency
Therapeutic value No estimate possible yet
Registration phase Registration application pending

Product

Active substance Tiratricol
Domain Neurological disorders
Reason of inclusion Generic
Main indication Neurological disorders other
Extended indication Treatment of monocarboxylate transporter 8 (MCT8) deficiency

Registration

Submission date October 2023
Expected Registration November 2024
Registration phase Registration application pending

Therapeutic value

Therapeutic value No estimate possible yet

Expected patient volume per year

Patiëntvolume is niet van toepassing bij generieke geneesmiddelen of biosimilars.

Expected cost per patient per year

Horizonscan vermeldt geen prijsinformatie van generieke geneesmiddelen of biosimilars om het eventueel beïnvloeden van de markt te voorkomen.

Potential total cost per year

Horizonscan vermeldt geen prijsinformatie van generieke geneesmiddelen of biosimilars om het eventueel beïnvloeden van de markt te voorkomen.

Off label use

There is currently nothing known about off label use.

Indication extension

There is currently nothing known about indication extensions.

Other information

There is currently no futher information available.